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REGENXBIO Announces Pipeline Expansion with RGX-181 Gene Therapy for CLN2 Form of Batten Disease

August 30, 2018

The expansion of Batten Disease treatment options is crucial to our community’s future. We are excited to share this announcement from REGENXBIO who plans to submit an IND for a new gene therapy for CLN2 in 2019. Because of news […]

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Sibling Highlight: Award Winning Poet Shalini Rana

June 20, 2018

In April, Shalini Rana, sibling of Shiv Rana CLN6, won third place in the Steger Poetry Prize. The Steger Poetry Prize is a prestigious award presented by celebrated poet Nikki Giovanni at Virginia Tech University. This year there were over 100 entries which were narrowed down to […]

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From Bench to Bedside, Getting to an FDA Approval

May 17, 2018

It is an exciting time for Batten research! As new research and potential trials are announced it is important that as a community that we understand the typical path research takes from the lab bench to patient bedside. Global Genes […]

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