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BDSRA Receives Genzyme Patient Advocacy Leadership (PAL) Award

September 30, 2013

Genzyme Announces Winners of Patient Advocacy Leadership (PAL) Awards CAMBRIDGE, Mass.–(BUSINESS WIRE)–September 30, 2013 Genzyme, a Sanofi company (EURONEXT: SAN and NYSE: SNY), today announced the recipients of the 2013 Genzyme Patient Advocacy Leadership (PAL) Awards. This global grant program […]

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BioMarin Pharmaceutical Inc. launches first phase of study in Hamburg, Germany

September 24, 2013

We applaud BioMarin Pharmaceutical Inc. for the official start of the Enzyme Replacement Therapy (ERT) trial in Germany. Here is the link for more details about the study: BioMarin doses first patient in CLN-2 study Contact Janet Nuttall at Jnuttall@bmrn.com for enrollment […]

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September issue of our newsletter the Illuminator

September 24, 2013

Check out the new edition of BDSRA newsletter to get updates on research, board nominations, donors and the family conference wrap-up September Illuminator  

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